Clinical Trial Insights

Soleno Therapeutics Announces Presentations on VYKAT™ XR for Prader-Willi Syndrome at ENDO 2025Clinical Trial Updates

Soleno Therapeutics Announces Presentations on VYKAT™ XR for Prader-Willi Syndrome at ENDO 2025

Soleno Therapeutics announced that two presentations featuring data on VYKAT™ XR (diazoxide choline) extended-release tablets for the treatment of hyp...

IDEAYA Biosciences Announces Positive Phase 2 Data for Darovasertib in Uveal MelanomaClinical Trial Updates

IDEAYA Biosciences Announces Positive Phase 2 Data for Darovasertib in Uveal Melanoma

IDEAYA Biosciences announced that data from a Phase 2 clinical trial of neoadjuvant darovasertib in primary uveal melanoma will be presented at the 20...

Spectral Medical's Tigris Trial Shows Positive Results for PMX in Endotoxic Septic ShockClinical Trial Updates

Spectral Medical's Tigris Trial Shows Positive Results for PMX in Endotoxic Septic Shock

Spectral Medical and Vantive announced positive topline results from the Tigris Phase 3 trial evaluating Polymyxin B Hemoadsorption (PMX) for endotoxi...

CASI Pharmaceuticals Announces Dose Escalation in Phase 1 CID-103 ITP StudyClinical Trial Updates

CASI Pharmaceuticals Announces Dose Escalation in Phase 1 CID-103 ITP Study

CASI Pharmaceuticals announced that the Safety Monitoring Committee (SMC) recommended dose escalation of CID-103, an anti-CD38 monoclonal antibody, to...

Spyre Therapeutics to Report Phase 1 Interim Results for SPY002 Anti-TL1A AntibodyClinical Trial Updates

Spyre Therapeutics to Report Phase 1 Interim Results for SPY002 Anti-TL1A Antibody

Spyre Therapeutics announced that it will report interim results from Phase 1 healthy volunteer trials for its SPY002 program, a novel half-life exten...

ITF Therapeutics Announces Positive Long-Term Givinostat Data for Duchenne Muscular DystrophyClinical Trial Updates

ITF Therapeutics Announces Positive Long-Term Givinostat Data for Duchenne Muscular Dystrophy

ITF Therapeutics announced the publication of positive long-term safety and efficacy data for givinostat in treating Duchenne muscular dystrophy (DMD)...

Taiho Oncology Presents Positive Data at ASCO 2025 Annual MeetingClinical Trial Updates

Taiho Oncology Presents Positive Data at ASCO 2025 Annual Meeting

Taiho Oncology announced new data to be presented at the 2025 American Society of Clinical Oncology (ASCO) Annual Meeting. Highlights include data on...

SystImmune to Present izalontamab brengitecan (iza-bren) Data at ASCO 2025Clinical Trial Updates

SystImmune to Present izalontamab brengitecan (iza-bren) Data at ASCO 2025

SystImmune, Inc. announced that data from clinical trials evaluating izalontamab brengitecan (iza-bren), an EGFRxHER3 bispecific antibody-drug conjuga...

ImCheck Reports High Remission Rates in AML Patients with ICT01 Combination TherapyClinical Trial Updates

ImCheck Reports High Remission Rates in AML Patients with ICT01 Combination Therapy

ImCheck Therapeutics announced positive interim data from its Phase I/II EVICTION study evaluating ICT01, a γ9δ2 T-cell activator, in combination with...

TauGen Files Patent Application for Novel TBI Drug CandidatesClinical Trial Updates

TauGen Files Patent Application for Novel TBI Drug Candidates

TauGen, LLC, in collaboration with CereMark Pharma, has filed a US patent application for a new class of drug candidates targeting traumatic brain inj...

Cantargia's CAN10 Shows Promise in Inhibiting Vascular InflammationClinical Trial Updates

Cantargia's CAN10 Shows Promise in Inhibiting Vascular Inflammation

Cantargia AB announced promising preclinical results for CAN10, an antibody targeting IL1RAP, in vascular inflammation models. The study, published i...

Telomir Pharmaceuticals' Telomir-1 Shows Promise in Preventing Cellular Aging in ProgeriaClinical Trial Updates

Telomir Pharmaceuticals' Telomir-1 Shows Promise in Preventing Cellular Aging in Progeria

Telomir Pharmaceuticals announced preclinical data showing its lead candidate, Telomir-1, prevented cellular aging in human progeria cell lines. Telo...

Immix Biopharma's NXC-201 Shows Promising Results for Relapsed/Refractory AL AmyloidosisClinical Trial Updates

Immix Biopharma's NXC-201 Shows Promising Results for Relapsed/Refractory AL Amyloidosis

Immix Biopharma announced positive results from its Phase 1/2 NEXICART-2 clinical trial of NXC-201, a sterically-optimized BCMA-targeted CAR-T cell th...

Tenaya Therapeutics Receives Positive Safety Reviews for TN-201 and TN-401 Gene Therapy TrialsClinical Trial Updates

Tenaya Therapeutics Receives Positive Safety Reviews for TN-201 and TN-401 Gene Therapy Trials

Tenaya Therapeutics announced positive safety reviews from independent Data Safety and Monitoring Boards (DSMBs) for its two cardiovascular gene thera...

Ascletis Initiates Phase IIa Trial of Oral GLP-1R Agonist ASC30 for ObesityClinical Trial Updates

Ascletis Initiates Phase IIa Trial of Oral GLP-1R Agonist ASC30 for Obesity

Ascletis Pharma announced the first participants have been dosed in a Phase IIa clinical trial (NCT07002905) evaluating ASC30, a novel small molecule ...

Tevogen Updates Development of AI-Powered EBV-Specific T Cell TherapyClinical Trial Updates

Tevogen Updates Development of AI-Powered EBV-Specific T Cell Therapy

Tevogen Bio Holdings Inc. announced an update on its development of a cytotoxic T lymphocyte (CTL) therapy targeting Epstein-Barr virus (EBV)-associat...

Immunic Reports Positive Long-Term Data for Vidofludimus Calcium in MSClinical Trial Updates

Immunic Reports Positive Long-Term Data for Vidofludimus Calcium in MS

Immunic, Inc. announced positive long-term open-label extension (OLE) data from its Phase 2 EMPhASIS trial of vidofludimus calcium (IMU-838) in relaps...

Tiziana Life Sciences Highlights Intranasal Foralumab for Moderate Alzheimer's DiseaseClinical Trial Updates

Tiziana Life Sciences Highlights Intranasal Foralumab for Moderate Alzheimer's Disease

Tiziana Life Sciences announced positive advancements in moderate Alzheimer's disease treatment using intranasal foralumab, a fully human anti-CD3 mon...

Cassava Sciences Reports Positive Preclinical Study of Simufilam for TSC-Related EpilepsyClinical Trial Updates

Cassava Sciences Reports Positive Preclinical Study of Simufilam for TSC-Related Epilepsy

Cassava Sciences announced positive preclinical results for simufilam in a mouse model of tuberous sclerosis complex (TSC)-related epilepsy. The stud...

Travere Therapeutics to Present New FILSPARI® (sparsentan) Data at the 15th International Podocyte ConferenceClinical Trial Updates

Travere Therapeutics to Present New FILSPARI® (sparsentan) Data at the 15th International Podocyte Conference

Travere Therapeutics announced it will present new data on FILSPARI (sparsentan) at the International Podocyte Conference. Data from the Phase 2 SPAR...

Indivior Advances Addex's GABAB PAM Program Through IND Enabling StudiesClinical Trial Updates

Indivior Advances Addex's GABAB PAM Program Through IND Enabling Studies

Indivior, partnering with Addex Therapeutics, successfully completed IND-enabling studies for a GABAB positive allosteric modulator (PAM) targeting su...

Updated Elacestrant Data Highlights Combinability in Metastatic Breast CancerClinical Trial Updates

Updated Elacestrant Data Highlights Combinability in Metastatic Breast Cancer

Menarini Group presented updated data from the Phase 1b/2 ELEVATE study at ASCO 2025, showcasing the efficacy and safety of elacestrant (ORSERDU®) in ...

Airiver Medical Receives FDA IDE Approval for Pivotal Clinical Study of Airiver Pulmonary Drug Coated BalloonClinical Trial Updates

Airiver Medical Receives FDA IDE Approval for Pivotal Clinical Study of Airiver Pulmonary Drug Coated Balloon

Airiver Medical announced that it has received Investigational Device Exemption (IDE) approval from the FDA to conduct a pivotal clinical trial of its...

VYNE Therapeutics' Phase 2b Repibresib Gel Trial for Vitiligo Misses Primary EndpointClinical Trial Updates

VYNE Therapeutics' Phase 2b Repibresib Gel Trial for Vitiligo Misses Primary Endpoint

VYNE Therapeutics announced topline results from its Phase 2b trial evaluating Repibresib gel in nonsegmental vitiligo. The trial, involving 177 subje...

Innate Pharma's Abstracts Selected for ASCO 2025 Annual MeetingClinical Trial Updates

Innate Pharma's Abstracts Selected for ASCO 2025 Annual Meeting

Innate Pharma announced that four abstracts featuring its clinical-stage drugs will be presented at the American Society of Clinical Oncology (ASCO) 2...

Vaxart's Second-Generation Norovirus Vaccine Shows Significantly Increased Antibody Responses in Phase 1 TrialClinical Trial Updates

Vaxart's Second-Generation Norovirus Vaccine Shows Significantly Increased Antibody Responses in Phase 1 Trial

Vaxart, Inc. announced positive topline results from a Phase 1 clinical trial evaluating its second-generation oral pill norovirus vaccine. The trial...

CeleCor Therapeutics Announces Positive Phase 3 Results for Disaggpro in Heart Attack PatientsClinical Trial Updates

CeleCor Therapeutics Announces Positive Phase 3 Results for Disaggpro in Heart Attack Patients

CeleCor Therapeutics announced positive topline results from its Phase 3 CeleBrate trial evaluating Disaggpro™ (zalunfiban) for heart attack treatment...

Vial Initiates Phase 1 Trial of Subcutaneous Half-Life Extended Anti-TL1A Antibody for IBDClinical Trial Updates

Vial Initiates Phase 1 Trial of Subcutaneous Half-Life Extended Anti-TL1A Antibody for IBD

Vial, a clinical-stage biotechnology company, announced the first-in-human dosing of its novel, subcutaneous, half-life extended monoclonal antibody t...

Invivyd Announces U.S. IND Clearance and FDA Alignment for VYD2311 COVID Prevention ProgramClinical Trial Updates

Invivyd Announces U.S. IND Clearance and FDA Alignment for VYD2311 COVID Prevention Program

Invivyd announced that the FDA has cleared its IND application and provided feedback to advance its REVOLUTION clinical program for VYD2311, a vaccine...

Vor Bio Announces Positive Phase 3 Results of Telitacicept in Systemic Lupus Erythematosus Published in NEJMClinical Trial Updates

Vor Bio Announces Positive Phase 3 Results of Telitacicept in Systemic Lupus Erythematosus Published in NEJM

Vor Bio announces the publication of positive results from a Phase 3 trial in China evaluating telitacicept for systemic lupus erythematosus (SLE) in ...

AskBio Announces Positive 12-Month Data from Phase 1 Trial of AB-1002 Gene Therapy for Congestive Heart Failure in Nature MedicineClinical Trial Updates

AskBio Announces Positive 12-Month Data from Phase 1 Trial of AB-1002 Gene Therapy for Congestive Heart Failure in Nature Medicine

AskBio, a subsidiary of Bayer AG, announced the publication of 12-month data from its Phase 1 trial of AB-1002 gene therapy for congestive heart failu...

KALA BIO Completes Enrollment in CHASE Trial for KPI-012 in Persistent Corneal Epithelial DefectClinical Trial Updates

KALA BIO Completes Enrollment in CHASE Trial for KPI-012 in Persistent Corneal Epithelial Defect

KALA BIO announced the completion of patient enrollment in the CHASE Phase 2b clinical trial evaluating KPI-012, a human mesenchymal stem cell secreto...

4B Technologies Announces Positive Phase 1 Results for Novel Non-Opioid Chronic Pain TherapyClinical Trial Updates

4B Technologies Announces Positive Phase 1 Results for Novel Non-Opioid Chronic Pain Therapy

4B Technologies announced positive topline results from a Phase 1 study of 4B03-04, a humanized monoclonal antibody for chronic pain. The trial demon...

AB Science Announces Initial Phase 1 Data for AB8939 and Venetoclax Combination in Refractory or Relapsed Acute Myeloid LeukemiaClinical Trial Updates

AB Science Announces Initial Phase 1 Data for AB8939 and Venetoclax Combination in Refractory or Relapsed Acute Myeloid Leukemia

AB Science SA announced initial Phase 1 data for the combination of AB8939 with venetoclax for treating refractory or relapsed acute myeloid leukemia ...

AbbVie Announces Positive Phase 3 Results for Upadacitinib (RINVOQ®) in VitiligoClinical Trial Updates

AbbVie Announces Positive Phase 3 Results for Upadacitinib (RINVOQ®) in Vitiligo

AbbVie announced positive topline results from two replicate Phase 3 studies evaluating upadacitinib (RINVOQ®) in adult and adolescent patients with n...

Aicuris' Pritelivir Meets Primary Endpoint in Phase 3 Trial for Refractory Herpes Simplex Virus in Immunocompromised PatientsClinical Trial Updates

Aicuris' Pritelivir Meets Primary Endpoint in Phase 3 Trial for Refractory Herpes Simplex Virus in Immunocompromised Patients

Aicuris Anti-infective Cures AG announced positive results from its Phase 3 trial (PRIOH-1) of pritelivir for treating refractory Herpes Simplex Virus...

Ascentage Pharma's Lisaftoclax Shows Promise in Venetoclax-Refractory Patients; ASCO 2025 PresentationClinical Trial Updates

Ascentage Pharma's Lisaftoclax Shows Promise in Venetoclax-Refractory Patients; ASCO 2025 Presentation

Ascentage Pharma announced positive clinical data for lisaftoclax, a Bcl-2 inhibitor, and alrizomadlin, an MDM2-p53 inhibitor. Data from a Phase 1b/2...

Candel Therapeutics to Present CAN-2409 Data at SITC 2025Clinical Trial Updates

Candel Therapeutics to Present CAN-2409 Data at SITC 2025

Candel Therapeutics will present data from its enLIGHTEN™ Discovery Platform and CAN-2409 program in non-small cell lung cancer (NSCLC) at the SITC 20...

ITM to Present COMPETE Trial Data at SNMMI 2025 Annual MeetingClinical Trial Updates

ITM to Present COMPETE Trial Data at SNMMI 2025 Annual Meeting

ITM Isotope Technologies Munich SE announced that it will present further analysis from its completed Phase 3 COMPETE trial at the SNMMI 2025 annual m...

TG Therapeutics Completes Enrollment in Phase 3 ENHANCE Trial of Simplified Dosing for BRIUMVI in Multiple SclerosisClinical Trial Updates

TG Therapeutics Completes Enrollment in Phase 3 ENHANCE Trial of Simplified Dosing for BRIUMVI in Multiple Sclerosis

TG Therapeutics announced the completion of enrollment in the Phase 3 ENHANCE trial, which is evaluating a simplified dosing schedule for BRIUMVI (ubl...

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