Clinical Trial Insights

ITF Therapeutics Announces Positive Long-Term Givinostat Data for Duchenne Muscular DystrophyClinical Trial Updates

ITF Therapeutics Announces Positive Long-Term Givinostat Data for Duchenne Muscular Dystrophy

ITF Therapeutics announced the publication of positive long-term safety and efficacy data for givinostat in treating Duchenne muscular dystrophy (DMD)...

Cantargia's CAN10 Shows Promise in Inhibiting Vascular InflammationClinical Trial Updates

Cantargia's CAN10 Shows Promise in Inhibiting Vascular Inflammation

Cantargia AB announced promising preclinical results for CAN10, an antibody targeting IL1RAP, in vascular inflammation models. The study, published i...

Immix Biopharma's NXC-201 Shows Promising Results for Relapsed/Refractory AL AmyloidosisClinical Trial Updates

Immix Biopharma's NXC-201 Shows Promising Results for Relapsed/Refractory AL Amyloidosis

Immix Biopharma announced positive results from its Phase 1/2 NEXICART-2 clinical trial of NXC-201, a sterically-optimized BCMA-targeted CAR-T cell th...

Ascletis Initiates Phase IIa Trial of Oral GLP-1R Agonist ASC30 for ObesityClinical Trial Updates

Ascletis Initiates Phase IIa Trial of Oral GLP-1R Agonist ASC30 for Obesity

Ascletis Pharma announced the first participants have been dosed in a Phase IIa clinical trial (NCT07002905) evaluating ASC30, a novel small molecule ...

Immunic Reports Positive Long-Term Data for Vidofludimus Calcium in MSClinical Trial Updates

Immunic Reports Positive Long-Term Data for Vidofludimus Calcium in MS

Immunic, Inc. announced positive long-term open-label extension (OLE) data from its Phase 2 EMPhASIS trial of vidofludimus calcium (IMU-838) in relaps...

Cassava Sciences Reports Positive Preclinical Study of Simufilam for TSC-Related EpilepsyClinical Trial Updates

Cassava Sciences Reports Positive Preclinical Study of Simufilam for TSC-Related Epilepsy

Cassava Sciences announced positive preclinical results for simufilam in a mouse model of tuberous sclerosis complex (TSC)-related epilepsy. The stud...

Indivior Advances Addex's GABAB PAM Program Through IND Enabling StudiesClinical Trial Updates

Indivior Advances Addex's GABAB PAM Program Through IND Enabling Studies

Indivior, partnering with Addex Therapeutics, successfully completed IND-enabling studies for a GABAB positive allosteric modulator (PAM) targeting su...

Airiver Medical Receives FDA IDE Approval for Pivotal Clinical Study of Airiver Pulmonary Drug Coated BalloonClinical Trial Updates

Airiver Medical Receives FDA IDE Approval for Pivotal Clinical Study of Airiver Pulmonary Drug Coated Balloon

Airiver Medical announced that it has received Investigational Device Exemption (IDE) approval from the FDA to conduct a pivotal clinical trial of its...

Innate Pharma's Abstracts Selected for ASCO 2025 Annual MeetingClinical Trial Updates

Innate Pharma's Abstracts Selected for ASCO 2025 Annual Meeting

Innate Pharma announced that four abstracts featuring its clinical-stage drugs will be presented at the American Society of Clinical Oncology (ASCO) 2...

CeleCor Therapeutics Announces Positive Phase 3 Results for Disaggpro in Heart Attack PatientsClinical Trial Updates

CeleCor Therapeutics Announces Positive Phase 3 Results for Disaggpro in Heart Attack Patients

CeleCor Therapeutics announced positive topline results from its Phase 3 CeleBrate trial evaluating Disaggpro™ (zalunfiban) for heart attack treatment...

Invivyd Announces U.S. IND Clearance and FDA Alignment for VYD2311 COVID Prevention ProgramClinical Trial Updates

Invivyd Announces U.S. IND Clearance and FDA Alignment for VYD2311 COVID Prevention Program

Invivyd announced that the FDA has cleared its IND application and provided feedback to advance its REVOLUTION clinical program for VYD2311, a vaccine...

AskBio Announces Positive 12-Month Data from Phase 1 Trial of AB-1002 Gene Therapy for Congestive Heart Failure in Nature MedicineClinical Trial Updates

AskBio Announces Positive 12-Month Data from Phase 1 Trial of AB-1002 Gene Therapy for Congestive Heart Failure in Nature Medicine

AskBio, a subsidiary of Bayer AG, announced the publication of 12-month data from its Phase 1 trial of AB-1002 gene therapy for congestive heart failu...

KALA BIO Completes Enrollment in CHASE Trial for KPI-012 in Persistent Corneal Epithelial DefectClinical Trial Updates

KALA BIO Completes Enrollment in CHASE Trial for KPI-012 in Persistent Corneal Epithelial Defect

KALA BIO announced the completion of patient enrollment in the CHASE Phase 2b clinical trial evaluating KPI-012, a human mesenchymal stem cell secreto...

Cizzle Bio Submits NIH Grant for Lung Cancer Biomarker Blood TestClinical Trial Updates

Cizzle Bio Submits NIH Grant for Lung Cancer Biomarker Blood Test

Cizzle Bio, a biotechnology company, submitted a grant application to the NIH for a two-year study validating its CIZ1B biomarker for early-stage lung...

Kazia Therapeutics Announces Preclinical Data on Paxalisib for Triple-Negative Breast CancerClinical Trial Updates

Kazia Therapeutics Announces Preclinical Data on Paxalisib for Triple-Negative Breast Cancer

Kazia Therapeutics announced the publication of preclinical research in Molecular Cancer Therapeutics demonstrating paxalisib's potential to overcome ...

AbbVie's VERONA Trial for Higher-Risk Myelodysplastic Syndromes Misses Primary EndpointClinical Trial Updates

AbbVie's VERONA Trial for Higher-Risk Myelodysplastic Syndromes Misses Primary Endpoint

AbbVie announced that the Phase 3 VERONA trial evaluating venetoclax in combination with azacitidine for newly diagnosed higher-risk myelodysplastic s...

Keros Therapeutics Initiates Phase 3 Trial of Elritercept for MDSClinical Trial Updates

Keros Therapeutics Initiates Phase 3 Trial of Elritercept for MDS

Keros Therapeutics announced the first patient dosing in the Phase 3 RENEW clinical trial of elritercept for adults with transfusion-dependent anemia ...

Clene Provides Regulatory Update on CNM-Au8 for ALS and MSClinical Trial Updates

Clene Provides Regulatory Update on CNM-Au8 for ALS and MS

Clene, Inc. announced a positive Type C meeting with the FDA regarding its statistical analysis plan for CNM-Au8 in ALS patients. The FDA provided co...

Kyverna Therapeutics Announces Conference Call on Interim Phase 2 Data of KYV-101 in Generalized Myasthenia GravisClinical Trial Updates

Kyverna Therapeutics Announces Conference Call on Interim Phase 2 Data of KYV-101 in Generalized Myasthenia Gravis

Kyverna Therapeutics will host a conference call to discuss interim data from the KYSA-6 Phase 2 clinical trial evaluating KYV-101 in generalized myas...

Aspire Biopharma Announces Positive Final Results for Sublingual Aspirin in Treating Heart AttacksClinical Trial Updates

Aspire Biopharma Announces Positive Final Results for Sublingual Aspirin in Treating Heart Attacks

Aspire Biopharma announced positive final results from a clinical trial evaluating its investigational sublingual aspirin product for suspected acute ...

LIfT BioSciences Presents Preclinical Data on Immunomodulatory Alpha Neutrophils (IMANs) for Solid TumorsClinical Trial Updates

LIfT BioSciences Presents Preclinical Data on Immunomodulatory Alpha Neutrophils (IMANs) for Solid Tumors

LIfT BioSciences announced the presentation of preclinical data on its first-in-class Immunomodulatory Alpha Neutrophils (IMANs) at the ISCT 2025 Annu...

Compass Pathways Announces Positive Phase 2 Results for COMP360 Psilocybin in PTSDClinical Trial Updates

Compass Pathways Announces Positive Phase 2 Results for COMP360 Psilocybin in PTSD

Compass Pathways announced the publication of positive Phase 2 results for their investigational drug COMP360, a synthetic psilocybin, in treating pos...

Legend Biotech Presents New Data on CARVYKTI® and Pipeline Candidates at ASCO, EHA, and ASGCTClinical Trial Updates

Legend Biotech Presents New Data on CARVYKTI® and Pipeline Candidates at ASCO, EHA, and ASGCT

Legend Biotech announced new data on CARVYKTI® (ciltacabtagene autoleucel), a CAR-T therapy for multiple myeloma, to be presented at ASCO and EHA. Lo...

Alafair Biosciences Initiates Multi-Center Study on VersaWrap® for Achilles Tendon RepairClinical Trial Updates

Alafair Biosciences Initiates Multi-Center Study on VersaWrap® for Achilles Tendon Repair

Alafair Biosciences announced the enrollment of the first patient in a multi-center study evaluating VersaWrap®, a bioresorbable tendon protector, for...

Lilly's Jaypirca (pirtobrutinib) Meets Primary Endpoint in Phase 3 CLL/SLL TrialClinical Trial Updates

Lilly's Jaypirca (pirtobrutinib) Meets Primary Endpoint in Phase 3 CLL/SLL Trial

Eli Lilly and Company announced positive topline results from the Phase 3 BRUIN CLL-314 clinical trial of Jaypirca (pirtobrutinib), a non-covalent BTK...

Coya Therapeutics Announces FDA Acceptance of IND for COYA 302 to Treat ALSClinical Trial Updates

Coya Therapeutics Announces FDA Acceptance of IND for COYA 302 to Treat ALS

Coya Therapeutics announced that the FDA has accepted its Investigational New Drug (IND) application for COYA 302, a biologic combination therapy for ...

Lilly's Oral GLP-1 Agonist, Orforglipron, Shows Significant Weight Loss in Phase 3 TrialClinical Trial Updates

Lilly's Oral GLP-1 Agonist, Orforglipron, Shows Significant Weight Loss in Phase 3 Trial

Eli Lilly and Company announced positive topline results from the Phase 3 ATTAIN-1 trial of orforglipron, an investigational oral GLP-1 receptor agoni...

Atossa Therapeutics Receives Positive FDA Feedback for (Z)-Endoxifen in Metastatic Breast CancerClinical Trial Updates

Atossa Therapeutics Receives Positive FDA Feedback for (Z)-Endoxifen in Metastatic Breast Cancer

Atossa Therapeutics announced positive feedback from the FDA regarding its proposed dose optimization trial of (Z)-endoxifen for ER+/HER2- metastatic ...

Lisata Therapeutics Announces Positive Preliminary Results from CENDIFOX Trial in Pancreatic CancerClinical Trial Updates

Lisata Therapeutics Announces Positive Preliminary Results from CENDIFOX Trial in Pancreatic Cancer

Lisata Therapeutics announced encouraging preliminary data from the Phase 1/2a CENDIFOX trial evaluating certepetide in combination with FOLFIRINOX fo...

CureGene's CG-0416 Shows Promise as Dual-Action Therapy for Obesity and MASHClinical Trial Updates

CureGene's CG-0416 Shows Promise as Dual-Action Therapy for Obesity and MASH

CureGene Pharmaceuticals announced preclinical data for its investigational drug, CG-0416, a liver-targeted thyroid hormone receptor beta (THR-β) prod...

MIRA Pharmaceuticals Completes Phase 1 Trial of Oral Ketamir-2 for Neuropathic PainClinical Trial Updates

MIRA Pharmaceuticals Completes Phase 1 Trial of Oral Ketamir-2 for Neuropathic Pain

MIRA Pharmaceuticals announced the successful completion of the single ascending dose (SAD) portion of its Phase 1 clinical trial for oral Ketamir-2, ...

AL-S Pharma Announces Positive Phase 2 Results for AP-101 in ALS TreatmentClinical Trial Updates

AL-S Pharma Announces Positive Phase 2 Results for AP-101 in ALS Treatment

AL-S Pharma reported positive topline results from its Phase 2 clinical trial of AP-101, a first-in-class monoclonal antibody targeting misfolded SOD1...

DATROWAY® Improves Overall and Progression-Free Survival in Metastatic Triple-Negative Breast CancerClinical Trial Updates

DATROWAY® Improves Overall and Progression-Free Survival in Metastatic Triple-Negative Breast Cancer

AstraZeneca and Daiichi Sankyo's DATROWAY® (datopotamab deruxtecan-dlnk) demonstrated statistically significant and clinically meaningful improvements...

4B Technologies Announces Positive Phase 1 Results for Novel Non-Opioid Chronic Pain TherapyClinical Trial Updates

4B Technologies Announces Positive Phase 1 Results for Novel Non-Opioid Chronic Pain Therapy

4B Technologies announced positive topline results from a Phase 1 study of 4B03-04, a humanized monoclonal antibody for chronic pain. The trial demon...

AB Science Announces Initial Phase 1 Data for AB8939 and Venetoclax Combination in Refractory or Relapsed Acute Myeloid LeukemiaClinical Trial Updates

AB Science Announces Initial Phase 1 Data for AB8939 and Venetoclax Combination in Refractory or Relapsed Acute Myeloid Leukemia

AB Science SA announced initial Phase 1 data for the combination of AB8939 with venetoclax for treating refractory or relapsed acute myeloid leukemia ...

AbbVie Announces Positive Phase 3 Results for Upadacitinib (RINVOQ®) in VitiligoClinical Trial Updates

AbbVie Announces Positive Phase 3 Results for Upadacitinib (RINVOQ®) in Vitiligo

AbbVie announced positive topline results from two replicate Phase 3 studies evaluating upadacitinib (RINVOQ®) in adult and adolescent patients with n...

Aicuris' Pritelivir Meets Primary Endpoint in Phase 3 Trial for Refractory Herpes Simplex Virus in Immunocompromised PatientsClinical Trial Updates

Aicuris' Pritelivir Meets Primary Endpoint in Phase 3 Trial for Refractory Herpes Simplex Virus in Immunocompromised Patients

Aicuris Anti-infective Cures AG announced positive results from its Phase 3 trial (PRIOH-1) of pritelivir for treating refractory Herpes Simplex Virus...

Ascentage Pharma's Lisaftoclax Shows Promise in Venetoclax-Refractory Patients; ASCO 2025 PresentationClinical Trial Updates

Ascentage Pharma's Lisaftoclax Shows Promise in Venetoclax-Refractory Patients; ASCO 2025 Presentation

Ascentage Pharma announced positive clinical data for lisaftoclax, a Bcl-2 inhibitor, and alrizomadlin, an MDM2-p53 inhibitor. Data from a Phase 1b/2...

Candel Therapeutics to Present CAN-2409 Data at SITC 2025Clinical Trial Updates

Candel Therapeutics to Present CAN-2409 Data at SITC 2025

Candel Therapeutics will present data from its enLIGHTEN™ Discovery Platform and CAN-2409 program in non-small cell lung cancer (NSCLC) at the SITC 20...

ITM to Present COMPETE Trial Data at SNMMI 2025 Annual MeetingClinical Trial Updates

ITM to Present COMPETE Trial Data at SNMMI 2025 Annual Meeting

ITM Isotope Technologies Munich SE announced that it will present further analysis from its completed Phase 3 COMPETE trial at the SNMMI 2025 annual m...

← PrevPage 4 of 8Next →

Get a Demo of the Enterprise AI & Knowledge Platform

Private by design. Speaks your language. Proven at scale